A. Mehta and B. Winchester, Lysosomal storage disorders, 2013.

K. E. Bergwerk, R. E. Falk, B. J. Glasgow, and Y. S. Rabinowitz, Corneal transplantation in a patient with mucopolysaccharidosis type VII (Sly disease), Ophthalmic Genet, vol.21, pp.17-20, 2000.

J. Muenzer, Overview of the mucopolysaccharidoses, Rheumatology, vol.50, issue.5, pp.4-12, 2011.

E. F. Neufeld, From serendipity to therapy, Annu Rev Biochem, vol.80, pp.1-15, 2011.

E. J. Kremer, Gene transfer to the central nervous system: current state of the art of the viral vectors, Curr Genomics, vol.6, pp.13-39, 2005.

Y. Kamata, T. Okuyama, M. Kosuga, O. 'hira, A. Kanaji et al., Adenovirus-mediated gene therapy for corneal clouding in mice with mucopolysaccharidosis type VII, Mol Ther, vol.4, pp.307-312, 2001.

T. S. Hnasko, F. A. Perez, A. D. Scouras, E. A. Stoll, S. D. Gale et al., Cre recombinase-mediated restoration of nigrostriatal dopamine in dopamine-deficient mice reverses hypophagia and bradykinesia, Proc Natl Acad Sci, vol.103, pp.8858-8863, 2006.

C. Soudais, N. Skander, and E. J. Kremer, Long-term in vivo transduction of neurons throughout the rat CNS using novel helper-dependent CAV-2 vectors, FASEB J, vol.18, pp.391-393, 2004.

M. Perreau and E. J. Kremer, Frequency, proliferation, and activation of human memory T cells induced by a nonhuman adenovirus, J Virol, vol.79, pp.14595-14605, 2005.

M. Perreau, M. C. Guerin, C. Drouet, and E. J. Kremer, Interactions between human plasma components and a xenogenic adenovirus vector: reduced immunogenicity during gene transfer, Mol Ther, vol.15, 1998.
URL : https://hal.archives-ouvertes.fr/hal-00400480

M. Perreau, F. Mennechet, N. Serratrice, J. N. Glasgow, D. T. Curiel et al., Contrasting effects of human, canine, and hybrid adenovirus vectors on the phenotypical and functional maturation of human dendritic cells: implications for clinical efficacy, J Virol, vol.81, pp.3272-3284, 2007.

E. H. Schuchman, T. K. Toroyan, M. E. Haskins, and R. J. Desnick, Characterization of the defective betaglucuronidase activity in canine mucopolysaccharidosis type VII, Enzyme, vol.42, pp.174-180, 1989.

E. J. Kremer, S. Boutin, M. Chillon, and O. Danos, Canine adenovirus vectors: an alternative for adenovirus-mediated gene transfer, J Virol, vol.74, pp.505-512, 2000.
DOI : 10.1128/jvi.74.1.505-512.2000

URL : https://jvi.asm.org/content/74/1/505.full.pdf

A. Cubizolle, N. Serratrice, N. Skander, M. A. Colle, S. Ibanes et al., Kremer, EJ. Corrective GUSB transfer to the canine mucopolysaccharidosis VII brain, Mol Ther, 2013.

L. Ariza, L. Gimenez-llort, A. Cubizolle, G. Pages, B. Garcia-lareu et al., Central nervous system delivery of helper-dependent canine adenovirus corrects neuropathology and behavior in mucopolysaccharidosis type VII mice
DOI : 10.1089/hum.2013.152

URL : http://europepmc.org/articles/pmc3955973?pdf=render

C. Soudais, S. Boutin, and E. J. Kremer, Characterization of cis-acting sequences involved in canine adenovirus packaging, Mol Ther, vol.3, pp.631-640, 2001.

W. S. Sly, B. A. Quinton, W. H. Mcalister, and D. L. Rimoin, Beta glucuronidase deficiency: report of clinical, radiologic, and biochemical features of a new mucopolysaccharidosis, J Pediatr, vol.82, pp.249-257, 1973.

C. Hippert, S. Ibanes, N. Serratrice, F. Court, F. Malecaze et al., Corneal transduction by intra-stromal injection of AAV vectors in vivo in the mouse and ex vivo in human explants, PLoS One, vol.7, 2012.

M. Sosnova, M. Bradl, and J. V. Forrester, CD34+ corneal stromal cells are bone marrow-derived and express hemopoietic stem cell markers, Stem Cells, vol.23, pp.507-515, 2005.

C. Soudais, S. Boutin, S. S. Hong, M. Chillon, O. Danos et al., Canine adenovirus type 2 attachment and internalization: coxsackievirus-adenovirus receptor, alternative receptors, and an RGD-independent pathway, J Virol, vol.74, pp.10639-10649, 2000.
DOI : 10.1128/jvi.74.22.10639-10649.2000

URL : https://hal.archives-ouvertes.fr/hal-00116153

J. M. Bergelson, J. A. Cunningham, G. Droguett, K. , E. A. Krithivas et al., Isolation of a common receptor for Coxsackie B viruses and adenoviruses 2 and 5, Science, vol.275, pp.1320-1323, 1997.

R. Tomko, R. Xu, and L. Philipson, HCAR and MCAR: the human and mouse cellular receptors for subgroup C adenoviruses and group B cocksakieviruses, Proc Natl Acad Sci, vol.94, pp.3352-3356, 1997.
DOI : 10.1073/pnas.94.7.3352

URL : http://www.pnas.org/content/94/7/3352.full.pdf

Y. Zhang and J. M. Bergelson, Adenovirus receptors, J Virol, vol.79, pp.12125-12131, 2005.
DOI : 10.1128/jvi.79.19.12125-12131.2005

URL : https://jvi.asm.org/content/79/19/12125.full.pdf

E. F. Neufeld, Lysosomal storage diseases, Annu Rev Biochem, vol.60, pp.257-280, 1991.

M. Sardiello, M. Palmieri, A. Di-ronza, D. L. Medina, M. Valenza et al., A gene network regulating lysosomal biogenesis and function, Science, vol.325, pp.473-477, 2009.
DOI : 10.1126/science.1174447

R. R. Mohan, J. C. Tovey, A. Sharma, and A. Tandon, Gene therapy in the cornea: 2005-present, Prog Retin Eye Res, vol.31, pp.43-64, 2012.
DOI : 10.1016/j.preteyeres.2011.09.001

URL : http://europepmc.org/articles/pmc3242872?pdf=render

T. Y. Lai, W. M. Chan, D. T. Liu, and D. S. Lam, Ranibizumab for retinal angiomatous proliferation in neovascular age-related macular degeneration, Graefes Arch Clin Exp Ophthalmol, vol.245, pp.1877-1880, 2007.
DOI : 10.1007/s00417-007-0679-1

H. Yu, J. Wu, H. Li, Z. Wang, X. Chen et al., Inhibition of corneal neovascularization by recombinant adenovirus-mediated sFlk-1 expression, Biochem Biophys Res Commun, vol.361, pp.946-952, 2007.
DOI : 10.1016/j.bbrc.2007.07.114

S. Saika, K. Ikeda, O. Yamanaka, T. Miyamoto, Y. Ohnishi et al., Expression of Smad7 in mouse eyes accelerates healing of corneal tissue after exposure to alkali, Am J Pathol, vol.166, pp.1405-1418, 2005.

S. D. Galiacy, P. Fournie, D. Massoudi, E. Ancele, J. C. Quintyn et al., Matrix metalloproteinase 14 overexpression reduces corneal scarring, Gene Ther, vol.18, pp.462-468, 2011.

K. A. Williams and D. J. Coster, Gene therapy for diseases of the cornea-a review, Clin Experiment Ophthalmol, vol.38, pp.93-103, 2010.

J. Alroy, M. Haskins, and D. E. Birk, Altered corneal stromal matrix organization is associated with mucopolysaccharidosis I, III and VI, Exp Eye Res, vol.68, pp.523-530, 1999.

V. Kalatzis, N. Serratrice, C. Hippert, O. Payet, C. Arndt et al., A temporospatial guide to the ocular anomalies in a cystinosis mouse model, Pediatr Res, vol.62, issue.2, pp.156-162, 2007.

G. Nesterova and W. Gahl, Nephropathic cystinosis: late complications of a multisystemic disease, Pediatr Nephrol, vol.23, pp.863-878, 2008.

S. U. Walkley, Pathogenic cascades in lysosomal disease-why so complex?, J Inherit Metab Dis, vol.32, pp.181-189, 2009.

R. Alba, A. Bosch, and M. Chillon, Gutless adenovirus: last-generation adenovirus for gene therapy, Gene Ther, vol.12, issue.1, pp.18-27, 2005.

A. Amalfitano and R. J. Parks, Separating fact from fiction: assessing the potential of modified adenovirus vectors for use in human gene therapy, Curr Gene Ther, vol.2, pp.111-133, 2002.

R. R. Mohan, A. E. Hutcheon, R. Choi, J. Hong, J. Lee et al., Apoptosis, necrosis, proliferation, and myofibroblast generation in the stroma following LASIK and PRK, Exp Eye Res, vol.76, pp.71-87, 2003.

A. P. Bemelmans, Y. Arsenijevic, and F. Majo, Efficient lentiviral gene transfer into corneal stroma cells using a femtosecond laser, Gene Ther, vol.16, pp.933-938, 2009.

M. E. Fini and B. M. Stramer, How the cornea heals: cornea-specific repair mechanisms affecting surgical outcomes, Cornea, vol.24, pp.2-11, 2005.

C. W. Sindt, B. Lay, H. Bouchard, and J. R. Kern, Rapid image evaluation system for corneal in vivo confocal microscopy, Cornea, vol.32, pp.460-465, 2013.

E. C. Carlson, C. Y. Liu, X. Yang, M. Gregory, B. Ksander et al., In vivo gene delivery and visualization of corneal stromal cells using an adenoviral vector and keratocyte-specific promoter, Invest Ophthalmol Vis Sci, vol.45, pp.2194-2200, 2004.

Y. Du, M. L. Funderburgh, M. M. Mann, N. Sundarraj, and J. L. Funderburgh, Multipotent stem cells in human corneal stroma, Stem Cells, vol.23, pp.1266-1275, 2005.

C. Vogler, N. Galvin, B. Levy, J. Grubb, J. Jiang et al., Transgene produces massive overexpression of human beta-glucuronidase in mice, lysosomal storage of enzyme, and straindependent tumors, Proc Natl Acad Sci U S A, vol.100, pp.2669-2673, 2003.

K. O. Orii, J. H. Grubb, C. Vogler, B. Levy, Y. Tan et al., Defining the pathway for Tat-mediated delivery of beta-glucuronidase in cultured cells and MPS VII mice, Mol Ther, vol.12, pp.345-352, 2005.

S. Tomatsu, K. O. Orii, C. Vogler, J. H. Grubb, E. M. Snella et al., Production of MPS VII mouse (Gus(tm(hE540A.mE536A)Sly)) doubly tolerant to human and mouse beta-glucuronidase, Hum Mol Genet, vol.12, pp.961-973, 2003.

J. H. Wolfe, M. S. Sands, N. Harel, M. A. Weil, M. K. Parente et al., Gene transfer of low levels of beta-glucuronidase corrects hepatic lysosomal storage in a large animal model of mucopolysaccharidosis VII, Mol Ther, vol.2, pp.552-561, 2000.

J. L. Ashworth, S. Biswas, E. Wraith, and L. Ic, Mucopolysaccharidoses and the eye, Surv Ophthalmol, vol.51, pp.1-17, 2006.

J. L. Ashworth, S. Biswas, E. Wraith, and L. Ic, The ocular features of the mucopolysaccharidoses, Eye, vol.20, pp.553-563, 2006.

J. Seok, H. S. Warren, A. G. Cuenca, M. N. Mindrinos, H. V. Baker et al., Genomic responses in mouse models poorly mimic human inflammatory diseases, Proc Natl Acad Sci U S A, vol.110, pp.3507-3512, 2013.